Orchard Therapeutics

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Orchard Therapeutics is a fully integrated commercial-stage biopharmaceutical company dedicated to transforming the lives of patients with serious and life-threatening rare diseases through innovative gene therapies.

Orchard’s portfolio of autologous ex vivo gene therapies includes Strimvelis, the first autologous ex vivo gene therapy approved by the European Medicines Agency for adenosine deaminase severe combined immunodeficiency (ADA-SCID). Additional programs for primary immune deficiencies, neurometabolic disorders and hemoglobinopathies include three advanced registrational studies for ADA-SCID, metachromatic leukodystrophy (MLD) and Wiskott-Aldrich syndrome (WAS), clinical programs for X-linked chronic granulomatous disease (X-CGD), transfusion dependent beta-thalassemia (TDBT) and Mucopolysaccharidosis type I (MPS-I), as well as an extensive preclinical pipeline.

Orchard currently has offices in the U.K. and the U.S., including London, San Francisco and Boston.

Orchard's pipeline

Orchard is utilising the potential of ex vivo autologous gene therapy to address severe and life-threatening inherited disorders, including primary immune deficiencies, inherited metabolic disorders and blood disorders.

Orchard’s pipeline includes Strimvelis®, the first ex vivo autologous gene therapy approved by the EMA in 2016, three advanced registrational studies for metachromatic leukodystrophy (MLD), ADA-SCID and Wiskott-Aldrich syndrome (WAS), clinical programs for X-linked chronic granulomatous disease (X-CGD), transfusion-dependent beta-thalassemia (TDT) and mucopolysaccharidosis type I (MPS-I), as well as an extensive preclinical pipeline.

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https://www.orchard-tx.com/
Type Public / Private
Headquarters London, UK

History

Controversies

Top 5 Recent Tweets

DateAuthorComment
November 25, 2020newsfilterioOrchard Therapeutics to Present at Piper Sandler 32nd Annual Virtual Healthcare Conference $ORTX https://t.co/5lLL9qkhBZ
November 24, 2020BioTuesdaysThe FDA cleared Orchard Therapeutics’ IND for OTL-200, a stem cell-based gene therapy for the treatment of metachro… https://t.co/mG4pnZxcat
November 24, 2020MarcJacksonLA$ORTX Orchard Therapeutics to Present at Piper Sandler 32nd Annual Virtual Healthcare Conference https://t.co/pDqkH151yl
November 24, 2020Cozino3$ortx

Orchard Therapeutics to Present at Piper Sandler 32nd Annual Virtual Healthcare Conference

https://t.co/5XgRqOIGRn


Top 5 Recent News Headlines

Orchard Therapeutics Reports Second Quarter 2019 Financial Results and Builds Momentum Ahead of Regulatory Filings

Metachromatic Leukodystrophy (MLD) MAA Submission and Initiation of ADA-SCID Rolling BLA Expected in the First Half of 2020; OTL-103 Recently Granted RMAT Designation for Wiskott-Aldrich Syndrome (WAS) MLD and Mucopolysaccharidosis Type I (MPS-I) Abstracts Accepted for Oral Presentations at SSIEM

Top 5 Lifetime Tweets

Top 5 Lifetime News Headlines

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